FDA Panel Endorses Gene Therapy For A Form Of Childhood Blindness

After many setbacks for genetic therapies, advisers to the Food and Drug Administration recommended approval of the first gene tr.....»»

Category: topSource: nprOct 12th, 2017

Seeing hope: FDA panel considers gene therapy for blindness

Advisers to the U.S. Food and Drug Administration will meet Thursday to consider whether to recommend approval of a gene therapy aimed at improving vision for some people with hereditary blindness......»»

Category: topSource: foxnewsOct 9th, 2017

FDA Panel Votes to Support Leukemia Gene-Therapy Treatment

A group of cancer experts voted unanimously to support U.S. regulatory approval for a first-of-its kind gene therapy targeting an aggressive form of leukemia in children and young adults......»»

Category: smallbizSource: wsjJul 13th, 2017

The Latest: FDA panel endorses potential 1st US gene therapy

The Latest on a Food and Drug Administration panel's review of a gene therapy treatment (all times local): 3:30 p.m......»»

Category: topSource: foxnewsJul 12th, 2017

New treatment for leukemia

Scientists at Stanford University have identified a molecule that can be targeted to cure leukemia, the most common form of cancer in childhood. The therapy is similar to but distinct from CD19-tar........»»

Category: topSource: thehindubusinesslineNov 21st, 2017

Gene Therapy Is Revolutionary Science That Can Cure Blindness. Is It Worth $1 Million a Pop?

One price watchdog group says no. 2017 has been a marquee year for gene therapy and medical technolog.....»»

Category: europeSource: fortuneNov 16th, 2017

Spark: A Big Win for Gene Therapy. So Why Is It Falling?

Shares of Spark Therapeutics are down today, despite winning the recommendation of a FDA advisory panel for its experimental gene therapy......»»

Category: blogSource: barronsOct 13th, 2017

Spark Therapeutics shares jump 7.5% after FDA committee backs blindness treatment

Shares of Spark Therapeutics Inc. surged 7.5% premarket Friday, after a U.S. Food and Drugs Administration advisory committee recommended approval of the company's gene therapy treatment for a rare eye disease that causes blindness. .....»»

Category: topSource: marketwatchOct 13th, 2017

A first-of-its-kind treatment for blindness just got one step closer to approval

AP A US Food and Drug Administration (FDA) advisory committee just gave a critical recommendation for a cutting-edge gene therapy.  The treatment, called Luxturna, treats Leber congenital amaurosis,&nbs.....»»

Category: topSource: businessinsiderOct 12th, 2017

FDA advisory panel recommends approval of Spark Therapeutics" gene therapy

A Food and Drug Administration advisory committee voted Thursday to recommend approval of Spark Therapeutics’ application for its experimental gene therapy developed to treat vision loss caused by an inherited retinal disease. The company, which .....»»

Category: topSource: bizjournalsOct 12th, 2017

Gene Therapy: How a New Cure for Blindness Reverses Retinal Dystrophy

The one-time treatment could restore eyesight to thousands of people......»»

Category: topSource: newsweekOct 12th, 2017

A gene therapy that could cure blindness is on the brink of getting approved (ONCE)

APA girl saw her mother's face for the first time. A boy tore through the aisles of Target, marveling at toys he never knew existed. A teen walked onto a stage and watched the stunned expressions of celebrity judges as he wowed "America's.....»»

Category: topSource: businessinsiderOct 10th, 2017

FDA considers gene therapy for blindness

FDA advisers will mull whether to recommend approval of a gene therapy that improved vision. It would be the first gene therapy in the U.S. for an inherited disease. .....»»

Category: topSource: usatodayOct 9th, 2017

Spark Therapeutics applies to market investigational therapy in Europe

The gene therapy company that spun out of Children's Hospital of Philadelphia is moving forward with a regulatory review of its treatment of an inherited disease that leads to blindness in Europe – laying the groundwork for the investigational therapy .....»»

Category: topSource: bizjournalsJul 31st, 2017

FDA panel backs Novartis" pioneering new cancer gene therapy

(Reuters) - Novartis AG's pioneering new cancer drug won enthusiastic support from a federal advisory panel on Wednesday, paving the way for approval of the first U.S. gene therapy......»»

Category: topSource: reutersJul 12th, 2017

Why Spark"s CEO says 2017 may be a "historic year" for his gene therapy company

Philadelphia gene therapy company Spark Therapeutics said it is in the final stages of completing its rolling biologics license application for its lead product: a one-time treatment for an inherited retinal disease that causes blindness in children.....»»

Category: topSource: bizjournalsFeb 22nd, 2017

Spark Therapeutics shares slide more than 40% after hemophilia data disappoint

Shares of gene therapy biotech Spark Therapeutics Inc. tumbled more than 40% in early trade Monday, after it reported data from trials of a hemophilia treatment that analysts said look less competitive than a rival product from BioMarin Pharma.....»»

Category: topSource: marketwatch4 hr. 24 min. ago

Why Spark Therapeutics stock price dropped by 40% this morning

Spark Therapeutics’ stock price plunged more than 40 percent Monday morning after the Philadelphia-based gene therapy company provided an update of its experimental hemophilia A treatment. Preliminary clinical data showed the gene therapy treat.....»»

Category: topSource: bizjournals4 hr. 39 min. ago

Lighting a Spark for Gene Therapy

A treatment for hemophilia B being developed by Spark Therapeutics and Pfizer gets highlighted in The New England Journal of Medicine......»»

Category: topSource: barronsDec 8th, 2017

Gene-therapy approach to hemophilia finds success in study, Spark stock surges

Spark Therapeutics Inc. stock surged Wednesday afternoon after the company announced positive results from a study of a gene-therapy approach to hemophilia. The drug, developed and tested in a collaboration with Pfizer Inc. , involves a sin.....»»

Category: topSource: marketwatchDec 6th, 2017

Gene therapy shows promise against blood-clotting disease

A study fuels hope that gene therapy can give long-lasting help and perhaps even cure the blood clotting disease called hemophilia......»»

Category: topSource: foxnewsDec 6th, 2017